- About Us
- Our Approach
- Patients & Providers
- Science & Pipeline
What We Do
Like limitless unique and manifold zebra-stripe patterns, our perspective on drug development assumes that there are boundless pathways and infinite possibilities through which difficult challenges can be overcome, always with the goal of making therapies available for people with rare diseases and significant unmet needs.
We specialize in advancing promising medicines that face complex clinical and regulatory challenges, balancing the science and data with patient need.
Our experience working with patient advocacy groups has given us deeper insights into patients and care partners, the challenges they face and how best we can work together with the rare disease community. We believe this will enable us to design better clinical programs that put the patient first.
Employing strategies that are outside the box, we push boundaries beyond rigid, one-track drug development paths that can limit access to therapeutics for people with rare diseases.
Leveraging our decades of experience in drug development, we have the know-how to develop therapies faster and a track record of overcoming challenging regulatory situations.
Rather than fitting data to a pre-determined narrative, we follow the data and re-assess our approach throughout the product development journey.
As adept data strategists, we analyze and then illuminate the meaning behind the data to produce compelling narratives that demonstrate the value of the therapeutics that people with rare diseases and the physicians overseeing their care so desperately need.
The importance of partnership
In rare disease, it takes a community effort to make real strides toward changing patient lives. We are committed to a patient-first approach coupled with outside-the-box thinking to advance promising product candidates to the people who desperately need them.
If you are a like-minded advocacy organization, foundation or biopharma company, you might be part of our herd.