Efficacy Results from a 12-month Double-blind Randomized Trial of Arimoclomol for the Treatment of Niemann-Pick Disease Type C — Presenting a Rescored 4-domain NPC Clinical Severity Scale
/wp-content/uploads/logo.svg00Jeff Lorber/wp-content/uploads/logo.svgJeff Lorber2025-02-07 11:59:292025-02-06 15:40:12Efficacy Results from a 12-month Double-blind Randomized Trial of Arimoclomol for the Treatment of Niemann-Pick Disease Type C — Presenting a Rescored 4-domain NPC Clinical Severity Scale
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