• News
  • Investors
  • Careers
  • Contact
  • X
  • About Us
    • Our Mission & Vision
    • The Zevra Story
    • Leadership
    • Board of Directors
  • Our Approach
    • What We Do
    • Partnering
  • Patients & Providers
    • Clinical Trials
    • Expanded Access Policy
    • Niemann-Pick Disease Type C
    • Urea Cycle Disorders
    • Vascular Ehlers-Danlos
    • Sleep Disorders
  • Products
    • MIPLYFFA ®
    • OLPRUVA ®
    • AZSTARYS ®
  • Science & Pipeline
    • Pipeline
    • Clinical Trials
    • Publications & Presentations
    • Medical Information
    • Investigator-Initiated Studies
  • Investors
    • Investor Relations
    • Events & Presentations
    • Stock Quote & Chart
    • Press Releases
    • Corporate Governance
    • SEC Filings
    • Contact
    • Email Alerts
  • Careers
    • Culture
    • Job Openings
  • Contact
    • [email protected]
    • 888.958.1253
    • Facebook
    • Twitter
    • LinkedIn
  • Home
  • Menu Menu

Our Approach

Unique patterns, boundless pathways and infinite possibilities . . .

What We Do

Like the limitless, unique and manifold zebra-stripe patterns, we see complexity as a call to push further for the benefit of the rare disease community that we serve.

In the face of difficult diseases, we don’t see barriers — we see opportunities to think differently. By staying true to our strategic pillars and driven by the urgency of patient needs, we specialize in advancing promising medicines that face unique development paths.

Our experience working with patient advocacy groups has given us deeper insights into patients and care partners, the challenges they face and how best we can work together with the rare disease community. We believe this will enable us to design better clinical programs that put the patient first.

Employing strategies that are outside the box, we push boundaries beyond rigid, one-track drug development paths that can limit access to therapeutics for people with rare diseases.

Leveraging our decades of experience in drug development, we have the know-how to develop therapies faster and a track record of overcoming challenging regulatory situations.

As a science driven company, rather than fitting data to a pre-determined narrative, we employ a data-driven, scientific approach to development, assessing and re-assessing our strategy  throughout the product development journey.

This commitment to data-driven decision making not only improves patient outcomes — it also establishes the foundation for building a leading, successful company.

The importance of partnership

In rare disease, it takes a community effort to make real strides toward changing patient lives. We are committed to a patient-first approach coupled with outside-the-box thinking to advance promising product candidates to the people who desperately need them.

If you are a like-minded advocacy organization, foundation or biopharma company, you might be part of our Zeal.

Contact us about partnering opportunities.

  • X
  • About Us
    • Our Mission & Vision
    • The Zevra Story
    • Leadership
    • Board of Directors
  • Our Approach
    • What We Do
    • Partnering
  • Patients & Providers
    • Clinical Trials
    • Expanded Access Policy
    • Niemann-Pick Disease Type C
    • Urea Cycle Disorders
    • Vascular Ehlers-Danlos
    • Sleep Disorders
  • Products
    • MIPLYFFA ®
    • OLPRUVA ®
    • AZSTARYS ®
  • Science & Pipeline
    • Pipeline
    • Clinical Trials
    • Publications & Presentations
    • Medical Information
    • Investigator-Initiated Studies
  • Investors
    • Investor Relations
    • Events & Presentations
    • Stock Quote & Chart
    • Press Releases
    • Corporate Governance
    • SEC Filings
    • Contact
    • Email Alerts
  • Careers
    • Culture
    • Job Openings
  • Contact
    • [email protected]
    • 888.958.1253
    • Facebook
    • Twitter
    • LinkedIn
  • Home

© 2025 Zevra Therapeutics. All rights reserved. | Privacy Policy | Notice at Collection | Your Privacy Choices | Terms of Use

Scroll to top

This site uses cookies. By continuing to browse the site, you are agreeing to our use of cookies.

Accept settingsHide notification onlySettings

Cookie and Privacy Settings



How we use cookies

We may request cookies to be set on your device. We use cookies to let us know when you visit our websites, how you interact with us, to enrich your user experience, and to customize your relationship with our website.

Click on the different category headings to find out more. You can also change some of your preferences. Note that blocking some types of cookies may impact your experience on our websites and the services we are able to offer.

Essential Website Cookies

These cookies are strictly necessary to provide you with services available through our website and to use some of its features.

Because these cookies are strictly necessary to deliver the website, refusing them will have impact how our site functions. You always can block or delete cookies by changing your browser settings and force blocking all cookies on this website. But this will always prompt you to accept/refuse cookies when revisiting our site.

We fully respect if you want to refuse cookies but to avoid asking you again and again kindly allow us to store a cookie for that. You are free to opt out any time or opt in for other cookies to get a better experience. If you refuse cookies we will remove all set cookies in our domain.

We provide you with a list of stored cookies on your computer in our domain so you can check what we stored. Due to security reasons we are not able to show or modify cookies from other domains. You can check these in your browser security settings.

Google Analytics Cookies

These cookies collect information that is used either in aggregate form to help us understand how our website is being used or how effective our marketing campaigns are, or to help us customize our website and application for you in order to enhance your experience.

If you do not want that we track your visit to our site you can disable tracking in your browser here:

Other external services

We also use different external services like Google Webfonts, Google Maps, and external Video providers. Since these providers may collect personal data like your IP address we allow you to block them here. Please be aware that this might heavily reduce the functionality and appearance of our site. Changes will take effect once you reload the page.

Google Webfont Settings:

Google Map Settings:

Google reCaptcha Settings:

Vimeo and Youtube video embeds:

Privacy Policy

You can read about our cookies and privacy settings in detail on our Privacy Policy Page.

Accept settingsHide notification only
Open Message Bar