Long-Term Effectiveness and Safety Evaluation of Arimoclomol Treatment in Patients With Niemann-Pick Disease Type C – Data From the Pivotal Study and Open-Label Extension
/wp-content/uploads/logo.svg00Jeff Lorber/wp-content/uploads/logo.svgJeff Lorber2025-07-11 09:22:182025-07-16 09:23:21Long-Term Effectiveness and Safety Evaluation of Arimoclomol Treatment in Patients With Niemann-Pick Disease Type C – Data From the Pivotal Study and Open-Label Extension
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