/wp-content/uploads/logo.svg00Jeff Lorber/wp-content/uploads/logo.svgJeff Lorber2024-11-11 10:45:062024-11-26 10:46:01Qualitative Assessment of the Validity and Standardization of the Swallow Domain in the 5-Domain Niemann-Pick disease type C (NPC) Clinical Severity Scale (5DNPCCSS)
/wp-content/uploads/logo.svg00Jeff Lorber/wp-content/uploads/logo.svgJeff Lorber2024-11-08 10:38:472024-11-26 10:51:22Arimoclomol Upregulates Expression of Genes Belonging to the Coordinated Lysosomal Expression and Regulation (CLEAR) Network
/wp-content/uploads/logo.svg00Jeff Lorber/wp-content/uploads/logo.svgJeff Lorber2024-09-05 12:48:122024-10-10 08:37:21Modeling the pharmacokinetics of phenylbutyrate in fed and fasted states
/wp-content/uploads/logo.svg00Jeff Lorber/wp-content/uploads/logo.svgJeff Lorber2024-09-05 12:47:262024-10-10 08:37:21Arimoclomol for the Treatment of NPC in a Real-World Setting: Long-Term Outcomes from an Expanded Access Program in the USA
/wp-content/uploads/logo.svg00Jeff Lorber/wp-content/uploads/logo.svgJeff Lorber2024-09-05 12:46:462024-10-10 08:37:21Arimoclomol Safety Profile in the Treatment of NPC in a Real-World Setting: Long-Term Data From an Expanded Access Program in the USA
/wp-content/uploads/logo.svg00Jeff Lorber/wp-content/uploads/logo.svgJeff Lorber2024-09-05 12:45:372024-10-10 08:37:21Long-term Efficacy and Safety Evaluation of Arimoclomol Treatment in Patients with Niemann Pick Type C – Data from 48 Months Open Label Trial
/wp-content/uploads/logo.svg00Jeff Lorber/wp-content/uploads/logo.svgJeff Lorber2024-09-05 12:30:152024-10-10 08:37:21Efficacy Results from a 12-month Double-blind Randomized Trial of Arimoclomol for Treatment of Niemann Pick Disease Type C – Presenting an Improved 4-Domain NPC Clinical Severity Scale
/wp-content/uploads/logo.svg00Jeff Lorber/wp-content/uploads/logo.svgJeff Lorber2024-04-15 15:31:342024-10-10 08:37:21Arimoclomol in adults with NPC in a real-world setting: Long-term data from an expanded access program in the USA
/wp-content/uploads/logo.svg00David Anderson/wp-content/uploads/logo.svgDavid Anderson2023-10-04 16:09:522024-10-10 08:37:21Evaluation of the Long-Term Effect of Arimoclomol in NPC – 48 Months Data from CT-ORZY-NPC-002
/wp-content/uploads/logo.svg00David Anderson/wp-content/uploads/logo.svgDavid Anderson2023-10-04 16:01:232024-10-10 08:37:21Real World Data Collection in Niemann-Pick Disease Type C – Data from Expanded Access Program with Arimoclomol
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