Efficacy results from a 12-month double-blind randomized trial of arimoclomol for treatment of Niemann-Pick disease type C (NPC): Presenting a rescored 4-domain NPC Clinical Severity Scale
/wp-content/uploads/logo.svg00Jeff Lorber/wp-content/uploads/logo.svgJeff Lorber2025-06-17 17:01:342025-06-17 17:01:34Efficacy results from a 12-month double-blind randomized trial of arimoclomol for treatment of Niemann-Pick disease type C (NPC): Presenting a rescored 4-domain NPC Clinical Severity Scale
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